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First received: May 08, 2023

Clinical Trial: Rollover Study From EXG-US-01

Study Status: NOT_YET_RECRUITING

Recruit Status: NOT_YET_RECRUITING

Condition: Telomere Biology Disorders With Bone Marrow Failure

Study Type: INTERVENTIONAL


Official Title: Long Term Follow-up Study in Patients With Telomere Biology Disorders With Bone Marrow Failure Who Completed Study EXG-US-01

Brief Summary: This is a long-term rollover follow-up study for Phase I/II study (Protocol EXG-US-01).

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