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First received: November 02, 2023

Clinical Trial: A Participant-mediated Observational Virtual Registry of Children With Achondroplasia in the United States

Study Status: Completed

Recruit Status: RECRUITING

Condition: Achondroplasia

Study Type: OBSERVATIONAL


Official Title: A Participant-mediated Observational Virtual Registry of Children With Achondroplasia in the United States

Brief Summary: This is an observational study of a pediatric cohort with achondroplasia in the United States.This cohort consists of both individuals treated and untreated with VOXZOGO™.Study enrollment started in February 2023.The projected total duration of the study is approximately 5 years, with the duration of individual prospective follow-up differing depending on the time of enrollment.The study duration may be extended based on decisions by the study sponsor.Data will be collected in two formats:Participant-mediated…

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